Inhibition of acid sphingomyelinase increases SMN levels and connects sphingolipid metabolism to Spinal Muscular Atrophy

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2025-09
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Brokate Llanos, Ana
Beltran Perelló, Maria
Garzón, Andrés
Garcera, AnaGarcera, Ana - ORCID ID
Miralles, María
Celma Nos, Ferrán
Campoy López, Alejandro
Soler i Tatché , Rosa Ma.
Muñoz, Manuel
Pérez Pulido, Antonio
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